Events

Upcoming Events

ATMP Webinar: A Practical Primer for Clinical Coordinators, Nurses & Pharmacists

June 15, 2026 | 3pm - 4pm ET | Virtual
REGISTER HERE

This webinar is the first in a series organized under Key Initiative 1.3 of the RareKids-CAN strategic priority, ‘Strengthening Pediatric Rare Disease Clinical Trial Capacity and Advanced Therapy Medicinal Product Readiness.’

It provides a practical introduction to Advanced Therapy Medicinal Products (ATMPs) for clinical coordinators, nurses, pharmacists, and research staff working in pediatric rare disease trials. Participants will gain a foundational understanding of gene therapies, cell therapies, and antisense oligonucleotides (ASOs) and how these trials differ from non-ATMP products or trials. 

By the end of the session, participants will feel more confident explaining ATMPs to patients and families in clear, accessible language.

By the end of this session, participants will be able to:

  • Define ATMPs and distinguish between gene therapy, cell therapy, and ASOs

  • Describe how ATMPs differ from traditional therapies (small molecules, biologics, etc)

  • Explain, at a high level, how ATMPs work and are made

  • Recognize key operational considerations

  • Confidently explain ATMPs to patients and families in plain language

Past Events

June 2, 2026: From Evidence to Access: Do Lived and Clinical Experiences Shape HTA Decisions?

How do lived experiences and frontline clinical insights influence health technology assessment (HTA) decisions in rare diseases?

This panel explored how patient and clinician voices are integrated into evidence frameworks. Through real-world examples, the discussion explored how HTA decisions can be more meaningfully anchored in lived and clinical experience.

Rare Disease Day 2026

RareKids-Can’s pediatric research institutions and their affiliated hospitals hosted events throughout the day (and during the week leading up to it) to raise awareness for patients and families living with rare diseases, as well as the clinicians and researchers who support them.

May 14, 2026: Bill C-265 Webinar: Improving Access to Essential Medications in Canada

RareKids-CAN hosted a timely conversation with MP Marcus Powlowski (MP for Thunder Bay – Rainy River) alongside healthcare professionals and patient advocates from across Canada, on improving access to essential medications not currently available in the country..

Participants learned what the changes proposed in Bill C-265 could mean for patients, families, and healthcare providers.

March 24, 2025: RareKids-CAN Round Up: Overview, Updates, and Collaboration [VIRTUAL]

This virtual information session is an opportunity to:

  • Gain an overview of RareKids-CAN, including the current services we offer to support study teams

  • Learn about our deliverables and activities across each sub-platform and the Clinical Trial Operations and Coordinating Hub (CTOCH)

  • Share your feedback on the network

  • Build connections within the community